A 19-year-old with cystic fibrosis (CF) is aiming to run the London Marathon to raise money for charity and awareness for the ...

In two randomised phase 3 studies involving 480 participants aged 12 years and over, ivacaftor/tezacaftor/vanzacaftor was ...

Vertex Pharmaceuticals (NasdaqGS:VRTX) announced that its cystic fibrosis treatment, ALYFTREK®, had received regulatory approval from the UK's MHRA, a significant milestone in expanding its market ...

H.C. Wainwright analyst Ed Arce lowered the firm’s price target on Arcturus Therapeutics (ARCT) to $60 from $63 and keeps a Buy rating on the ...

However, when Brandon Blackmon, 26, captured photos of his wife, Rinley Blackmon, 24, following their daughter's birth in June 2024, he opted for a very different style. Instead of taking the ...

A boy with a love of trains has gone behind the scenes at a railway signalling hub as a birthday treat.Zach from Walsall has cystic fibrosis and autism and his family said he developed a fascination ...

The UK’s Medicines and Healthcare products Regulatory Agency (MHRA) has today approved Alyftrek (triple combination medicine ...

Sionna Therapeutics recently secured an initial public offering (IPO) of $191m on the Nasdaq stock exchange, signalling ...

Researchers trial inhalable gene therapy for cystic fibrosis, offering a potential breakthrough in treating the genetic lung ...

Approximately 1,000 new cases of Cystic Fibrosis are diagnosed each year that bring costly treatments to many families. The life-threatening genetic disorder is ...