In two randomised phase 3 studies involving 480 participants aged 12 years and over, ivacaftor/tezacaftor/vanzacaftor was ...

A 19-year-old with cystic fibrosis (CF) is aiming to run the London Marathon to raise money for charity and awareness for the ...

Vertex Pharmaceuticals (NasdaqGS:VRTX) announced that its cystic fibrosis treatment, ALYFTREK®, had received regulatory approval from the UK's MHRA, a significant milestone in expanding its market ...

H.C. Wainwright analyst Ed Arce lowered the firm’s price target on Arcturus Therapeutics (ARCT) to $60 from $63 and keeps a Buy rating on the ...

However, when Brandon Blackmon, 26, captured photos of his wife, Rinley Blackmon, 24, following their daughter's birth in June 2024, he opted for a very different style. Instead of taking the ...

The UK’s Medicines and Healthcare products Regulatory Agency (MHRA) has today approved Alyftrek (triple combination medicine ...

Sionna Therapeutics recently secured an initial public offering (IPO) of $191m on the Nasdaq stock exchange, signalling ...

Researchers trial inhalable gene therapy for cystic fibrosis, offering a potential breakthrough in treating the genetic lung ...

Approximately 1,000 new cases of Cystic Fibrosis are diagnosed each year that bring costly treatments to many families. The life-threatening genetic disorder is ...

Beth A. Smith, MD, has been appointed chair of the Department of Psychiatry in the Jacobs School of Medicine and Biomedical ...